WHAT IS THE GTX-102-001 STUDY?
 


A Clinical Study in Angelman Syndrome

A Clinical Study in Angelman Syndrome

This is a first in human study of an investigational antisense oligonucleotide (ASO) called “GTX-102” being evaluated in individuals with Angelman syndrome (AS). The clinical research study is sponsored by GeneTx Biotherapeutics, LLC.

What is the GTX-102-001 Study?


 

Copyright © 2020   |  KIK-AS Study  |   All Rights Reserved   |  Privacy  HIPAA  |  Terms & Conditions